Changes in motor units closely reflect disease severity in people with spinal muscular atrophy (SMA), suggesting potential ...

Alice Wong, a disability rights activist with spinal muscular atrophy who died in November, left behind a legacy of advocacy ...

Columnist Connie Chandler is often asked how her parents raised two children with SMA, so she decided to find out for herself ...

Evrysdi can stabilize motor function, improve swallowing ability, ease fatigue, and improve life quality for adults with SMA, ...

SMA children who can't walk have weaker upper leg bones than kids with cerebral palsy who are nonambulatory, a comparative ...

Let's have more conversations about intersecting identities and diverse representation in films and musicals, says columnist.

Columnist Connie Chandler may have limited control over her physical abilities, but she can always strengthen her faith and ...

Columnist Brianna Albers is not good at waiting. One might say she's terrible at it. Living with SMA, though, seems to bring a lot of it.

Discover the most-read SMA stories of 2025, featuring updates on the gene therapy Zolgensma, next-generation treatments, and diet research.

The gene therapy Zolgensma (onasemnogene abeparvovec-xioi) has been newly approved to treat patients with spinal muscular atrophy (SMA) through intravenous (IV) delivery, meaning systemically. However ...

After a “constructive and collaborative in-person” meeting with the U.S. Food and Drug Administration (FDA), Scholar Rock is now planning to once again seek approval of its muscle-strengthening agent ...

For whatever reason, society loves to infantilize disabled people. It’s practically a hobby for some people, be they medical professionals or middle-aged pedestrians looking to test their comedy ...